✦ LIBER ✦

Progress in gene therapy for Duchenne muscular dystrophy

✍ Scribed by Paula R. Clemens; F Jason Duncan

Book ID: 107543113
Publisher: Springer
Year: 2001
Tongue: English
Weight: 396 KB
Volume: 1
Category: Article
ISSN: 1528-4042
DOI: 10.1007/s11910-001-0080-0

No coin nor oath required. For personal study only.

📜 SIMILAR VOLUMES

Gene therapy flexes muscle : A European

Gene therapy flexes muscle : A European Society of Gene Therapy commentary on progress in gene therapy for Duchenne muscular dystrophy and amyotrophic lateral sclerosis

✍ Thierry VandenDriessche 📂 Article 📅 2005 🏛 John Wiley and Sons 🌐 English ⚖ 45 KB

## Abstract This commentary highlights the promising results of recent studies in animal models of Duchenne muscular dystrophy and amyotrophic lateral sclerosis that have clearly demonstrated the potential of gene therapy for tackling these diseases. In the absence of effective drugs or other treat

Retroviral vectors for gene therapy of D

Retroviral vectors for gene therapy of Duchenne muscular dystrophy

✍ A. Fassati 📂 Article 📅 2000 🏛 Springer Milan 🌐 English ⚖ 31 KB

Gene therapy for duchenne dystrophy

✍ Andrew G. Engel 📂 Article 📅 1993 🏛 John Wiley and Sons 🌐 English ⚖ 240 KB 👁 1 views

Cell based therapy for duchenne muscular

Cell based therapy for duchenne muscular dystrophy

✍ Andrea Farini; Paola Razini; Silvia Erratico; Yvan Torrente; Mirella Meregalli 📂 Article 📅 2009 🏛 John Wiley and Sons 🌐 English ⚖ 159 KB

## Abstract Mutations in the dystrophin gene cause an X‐linked genetic disorder: Duchenne muscular dystrophy (DMD). Stem cell therapy is an attractive method to treat DMD because a small number of cells are required to obtain a therapeutic effect. Here, we discussed about multiple types of myogenic

The IVth workshop on Duchenne muscular d

The IVth workshop on Duchenne muscular dystrophy gene therapy

✍ K. Schwartz; F. Leterrier 📂 Article 📅 1999 🏛 John Wiley and Sons 🌐 English ⚖ 68 KB 👁 1 views

Therapeutics in Duchenne muscular dystro

Therapeutics in Duchenne muscular dystrophy

✍ Strober, Jonathan B. 📂 Article 📅 2006 🏛 American Society for Experimental NeuroTherapeutic 🌐 English ⚖ 169 KB

Duchenne muscular dystrophy (DMD) is a fatal disorder affecting approximately 1 in 3500 live born males, characterized by progressive muscle weakness. Several different strategies are being investigated in developing a cure for this disorder. Until a cure is found, therapeutic and supportive care is