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POM-001 Phase 1/2 Study of BMN 701, GILT-tagged Recombinant Human (rh) GAA in Late-Onset Pompe Disease: Preliminary Report

✍ Scribed by Barry Byrne; Bruce Barshop; Richard Barohn; Lindsay Falk; Michael Fox; William Lang; Michelle Lossius; Sean McCarthy; Jayesh Vora; Jonathon LeBowitz

Book ID: 116989526
Publisher: Elsevier Science
Year: 2012
Tongue: English
Weight: 55 KB
Volume: 105
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2011.11.040

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