Preliminary clinical efficacy and safety of BMN 701, GILT-tagged recombinant human acid alpha glucosidase (rhGAA), in late-onset Pompe disease: results of an extension study

✍ Scribed by Byrne, Barry; Barohn, Richard; Barshop, Bruce; Bratkovic, Drago; Desnuelle, Claude; Henderson, Robert; Hiwot, Tarekegn; Hughes, Derralynn; Laforet, Pascal; Mengel, Eugen; Roberts, Mark; Lang, William; LeBowitz, Jonathon

• Book ID: 122321778
• Publisher: Elsevier Science
• Year: 2014
• Tongue: English
• Weight: 50 KB
• Volume: 111
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2013.12.050