POM-001 phase 1/2 study of BMN 701, GILT-tagged recombinant human (rh) GAA in late-onset Pompe disease: Initial experience in 22 patients

✍ Scribed by Byrne, Barry; Barohn, Richard; Barshop, Bruce; Bratkovic, Drago; Desnuelle, Claude; Geberhiwot, Tarekegn; Hughes, Derralynn; Laforet, Pascal; Mengel, Eugen; Roberts, Mark; Lang, William; LeBowitz, Jonathan

• Book ID: 118733699
• Publisher: Elsevier Science
• Year: 2013
• Tongue: English
• Weight: 62 KB
• Volume: 108
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2012.11.048