We have recently described a chemotactic defect in severely afflicted Gaucher disease patients. Two of the patients were treated with low-dose intravenous enzyme replacement (Ceredase). Marked improvement in their hematological status, organomegaly, and growth was observed. In addition, their chemot
Enzyme replacement therapy for mild patients with Gaucher disease
โ Scribed by Ari Zimran; Yaron Ilan; Deborah Elstein
- Publisher
- John Wiley and Sons
- Year
- 2009
- Tongue
- English
- Weight
- 68 KB
- Volume
- 84
- Category
- Article
- ISSN
- 0361-8609
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