Biomarker responses to eliglustat, an investigational oral substrate reduction therapy (SRT) for Gaucher disease type 1 (GD1)

✍ Scribed by Peterschmitt, M. Judith; Lukina, Elena; Watman, Nora; Dragosky, Marta; Pastores, Gregory; Arreguin, Elsa Avila; Rosenbaum, Hanna; Zimran, Ari; Aguzzi, Rasha; Angell, Jennifer; Puga, Ana Cristina; Cox, Gerald

• Book ID: 122464827
• Publisher: Elsevier Science
• Year: 2013
• Tongue: English
• Weight: 58 KB
• Volume: 108
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2012.11.195