Eliglustat, an investigational oral therapy for Gaucher disease type 1 (GD1): Phase 2 results and assessment of patient responses and achievement of established therapeutic goals after 2 years of treatment

✍ Scribed by Marta Dragosky; Elena Lukina; Nora Watman; Gregory Pastores; Marcelo Iastrebner; Elsa Avila Arreguin; Hanna Rosenbaum; Mici Phillips; Mathilde Kaper; Dominique Bertin-Millet; Ana Cristina Puga; M. Judith Peterschmitt

• Book ID: 116989149
• Publisher: Elsevier Science
• Year: 2011
• Tongue: English
• Weight: 70 KB
• Volume: 102
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2010.11.052