Eliglustat, an investigational oral therapy for gaucher disease type 1 (GD1): Phase 2 results and assessment of patient responses and achievement of established therapeutic goals after 2 years of treatment

✍ Scribed by Ana Cristina Puga; Elena Lukina; Nora Watman; Marta Dragosky; Marcelo Lastrebner; Gregory Pastores; Elsa Avila Arreguin; Hanna Rosenbaum; Mici Phillips

• Book ID: 117984294
• Publisher: Elsevier Science
• Year: 2011
• Tongue: English
• Weight: 58 KB
• Volume: 102
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2010.11.124