## Abstract Niemann–Pick disease type C (NPC) is a progressive neurodegenerative disorder for which there is no effective treatment other than supportive therapy. Recently, the oral medication miglustat has been offered as a possible therapy aimed at reducing pathological substrate accumulation. Th
✦ LIBER ✦
Treatment of a child diagnosed with Niemann–Pick disease type C with miglustat: A case report in Brazil
✍ Scribed by M. L. F. Santos; S. Raskin; D. S. Telles; A. Löhr Junior; P. B. N. Liberalesso; S. C. Vieira; M. L. Cordeiro
- Publisher
- Springer
- Year
- 2008
- Tongue
- English
- Weight
- 268 KB
- Volume
- 31
- Category
- Article
- ISSN
- 0141-8955
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