Treatment of Niemann–Pick disease type C in two children with miglustat: Initial responses and maintenance of effects over 1

✍ Scribed by Y.-H. Chien; N.-C. Lee; L.-K. Tsai; A.-C. Huang; S.-F. Peng; S.-J. Chen; W.-L. Hwu

• Publisher: Springer
• Year: 2007
• Tongue: English
• Weight: 131 KB
• Volume: 30
• Category: Article
• ISSN: 0141-8955
• DOI: 10.1007/s10545-007-0630-y