## Abstract In the last years, much progress has been achieved in the field of lysosomal storage disorders. In the past, no specific treatment was available for the affected patients; management mainly consisted of supportive care and treatment of complications. As orphan drug regulations, however,
β¦ LIBER β¦
Therapeutic approaches for neuronopathic lysosomal storage disorders
β Scribed by Raphael Schiffmann
- Publisher
- Springer
- Year
- 2010
- Tongue
- English
- Weight
- 156 KB
- Volume
- 33
- Category
- Article
- ISSN
- 0141-8955
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