## Abstract In the last years, much progress has been achieved in the field of lysosomal storage disorders. In the past, no specific treatment was available for the affected patients; management mainly consisted of supportive care and treatment of complications. As orphan drug regulations, however,
Newborn screening for lysosomal storage disorders
β Scribed by Kimitoshi Nakamura; Kiyoko Hattori; Fumio Endo
- Publisher
- John Wiley and Sons
- Year
- 2011
- Tongue
- English
- Weight
- 115 KB
- Volume
- 157
- Category
- Article
- ISSN
- 1552-4868
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