Liver transplantation for propionic acid
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Roshni Vara; Charles Turner; Helen Mundy; Nigel D. Heaton; Mohammed Rela; Giorgi
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Article
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2011
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John Wiley and Sons
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English
โ 146 KB
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Propionic acidemia (PA) is a rare inherited disorder of branched chain amino acid metabolism; despite improvements in conventional medical management, the long-term outcome remains disappointing. Liver transplantation (LT) has been proposed to minimize the risk of further metabolic decompensations a