Phase I/II Trial of Adeno-Associated Virus–Mediated Alpha-Glucosidase Gene Therapy to the Diaphragm for Chronic Respiratory Failure in Pompe Disease: Initial Safety and Ventilatory Outcomes

✍ Scribed by Smith, Barbara K.; Collins, Shelley W.; Conlon, Thomas J.; Mah, Cathryn S.; Lawson, Lee Ann; Martin, Anatole D.; Fuller, David D.; Cleaver, Brian D.; Clément, Nathalie; Phillips, Dawn; Islam, Saleem; Dobjia, Nicole; Byrne, Barry J.

• Book ID: 120522076
• Publisher: Mary Ann Liebert
• Year: 2013
• Tongue: English
• Weight: 530 KB
• Volume: 24
• Category: Article
• ISSN: 1043-0342
• DOI: 10.1089/hum.2012.250