Phase I/II Trial of Adeno-associated Virus Acid-alpha-Glucosidase (AAV-GAA) Diaphragm Gene Therapy for Ventilatory Failure in Pompe Disease

✍ Scribed by Barry Byrne; Barbara Smith; Anatole Martin; Cathryn Mah; Lee Ann Lawson; Saleem Islam; Thomas Conlon; Dawn Phillips; Shelley Collins

• Book ID: 116989525
• Publisher: Elsevier Science
• Year: 2012
• Tongue: English
• Weight: 55 KB
• Volume: 105
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2011.11.039