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Non-viral transfer approaches for the gene therapy of mucopolysaccharidosis type II (Hunter syndrome)

✍ Scribed by R Tomanin; A Friso; S Alba; E Piller Puicher; C Mennuni; N La Monica; G Hortelano; F Zacchello; M Scarpa

Book ID: 114813314
Publisher: John Wiley and Sons
Year: 2007
Tongue: English
Weight: 186 KB
Volume: 91
Category: Article
ISSN: 0803-5253
DOI: 10.1111/j.1651-2227.2002.tb03119.x

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## Communicated by Francesco Giannelli Mucopolysaccharidosis type I1 (MI'S 11) is an X-chromosomal storage disorder due to deficiency of the lysosomal enzyme iduronate-2-sulfatase