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Investigational intrathecal (IT) enzyme replacement therapy for the severe form of Hunter syndrome (mucopolysaccharidosis type II, MPS II)

✍ Scribed by Muenzer, Joseph; Hendriksz, Christian J.; Stein, Margot B.; Fan, Zheng; Kearney, Shauna; Horton, Johan; Vijayaraghavan, Suresh; Perry, Victor; Santra, Saikat; Solanki, Guirish A.; Wang, Nan; Mascelli, Mary Ann; Pan, Luying; Sciarappa, Kenneth; Barbier, Ann J.

Book ID: 122206414
Publisher: Elsevier Science
Year: 2014
Tongue: English
Weight: 49 KB
Volume: 111
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2013.12.184

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