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MLP010 Pompe disease: early signs of benefit in a child with late-onset form following treatment with enzyme replacement therapy (ERT)

✍ Scribed by D. Lianou; D. Syrengelas; P. Poulopoulos; K. Kotsonis; A. Klimentopoulou; I. Mavridou; H. Michelakakis; K. Kassiou

Book ID: 114359564
Publisher: Elsevier Science
Year: 2007
Tongue: English
Weight: 47 KB
Volume: 11
Category: Article
ISSN: 1090-3798
DOI: 10.1016/s1090-3798(08)70510-5

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