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Survival and developmental milestones among Pompe registry patients with classic infantile-onset Pompe disease with different timing of initiation of treatment with enzyme replacement therapy (ERT)

✍ Scribed by Chien, Yin-Hsiu; van der Ploeg, Ans; Jones, Simon A.; Byrne, Barry; Vellodi, Ashok; Leslie, Nancy; Mengel, Eugen; Shankar, Suma; Tanpaiboon, Pranoot; Stockton, David W.; Hennermann, Julia B.; Devecseri, Zsuzsanna; Kempf, Judy; Keutzer, Joan; Kishnani, Priya S.

Book ID: 122185456
Publisher: Elsevier Science
Year: 2014
Tongue: English
Weight: 69 KB
Volume: 111
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2013.12.057

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