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Miglustat therapy in the French cohort of paediatric patients with Niemann-Pick disease type C

✍ Scribed by Bénédicte Héron, Vassili Valayannopoulos, Julien Baruteau, Brigitte Chabrol, Hélène Ogier, Philippe Latour, Dries Dobbelaere, Didier Eyer, François Labarthe, Hélène Maurey, Jean-Marie Cuisset, Thierry Billette de Villemeur, Frédéric Sedel, Marie T Vanier

Book ID: 119911426
Publisher: BioMed Central
Year: 2012
Tongue: English
Weight: 426 KB
Volume: 7
Category: Article
ISSN: 1750-1172
DOI: 10.1186/1750-1172-7-36

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