Miglustat in patients with Niemann-Pick disease Type C (NP-C): A multicenter observational retrospective cohort study

✍ Scribed by M. Pineda; J.E. Wraith; E. Mengel; F. Sedel; W.-L. Hwu; M. Rohrbach; B. Bembi; M. Walterfang; G.C. Korenke; T. Marquardt; C. Luzy; R. Giorgino; M.C. Patterson

• Book ID: 116988691
• Publisher: Elsevier Science
• Year: 2009
• Tongue: English
• Weight: 413 KB
• Volume: 98
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2009.07.003