Gene therapy for lysosomal storage disea
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N. Matthew Ellinwood; Charles H. Vite; Mark E. Haskins
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Article
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2004
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John Wiley and Sons
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English
β 596 KB
## Abstract There are more than 40 different forms of inherited lysosomal storage diseases (LSDs) known to occur in humans and the aggregate incidence has been estimated to approach 1 in 7000 live births. Most LSDs are associated with high morbidity and mortality and represent a significant burden