𝔖 Bobbio Scriptorium
✦   LIBER   ✦

Gene therapy approaches for lysosomal storage disorders, a good model for the treatment of mendelian diseases

✍ Scribed by Rosella Tomanin; Alessandra Zanetti; Eva Zaccariotto; Francesca D’Avanzo; Cinzia M Bellettato; Maurizio Scarpa

Book ID
114817358
Publisher
John Wiley and Sons
Year
2012
Tongue
English
Weight
300 KB
Volume
101
Category
Article
ISSN
0803-5253

No coin nor oath required. For personal study only.

📜 SIMILAR VOLUMES

Gene therapy for lysosomal storage disea
Gene therapy for lysosomal storage diseases: the lessons and promise of animal models
✍ N. Matthew Ellinwood; Charles H. Vite; Mark E. Haskins 📂 Article 📅 2004 🏛 John Wiley and Sons 🌐 English ⚖ 596 KB

## Abstract There are more than 40 different forms of inherited lysosomal storage diseases (LSDs) known to occur in humans and the aggregate incidence has been estimated to approach 1 in 7000 live births. Most LSDs are associated with high morbidity and mortality and represent a significant burden