Immune responses to dystrophin: implications for gene therapy of Duchenne muscular dystrophy
โ Scribed by Ferrer, A; Wells, K E; Wells, D J
- Book ID
- 110038748
- Publisher
- Nature Publishing Group
- Year
- 2000
- Tongue
- English
- Weight
- 237 KB
- Volume
- 7
- Category
- Article
- ISSN
- 0969-7128
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๐ SIMILAR VOLUMES
There are rare female patients who suffer from Duchenne or Becker muscular dystrophy because they carry an X;autosome translocation with a breakpoint in the dystrophin gene. We have defined the positions of seven of these breakpoints with respect to exon-containing HindIII fragments detected by dyst
## Abstract This commentary highlights the promising results of recent studies in animal models of Duchenne muscular dystrophy and amyotrophic lateral sclerosis that have clearly demonstrated the potential of gene therapy for tackling these diseases. In the absence of effective drugs or other treat