## Abstract ## Introduction: Enzyme replacement therapy (ERT) in ultra‐orphan Pompe disease generates anti‐rhGAA antibodies, which may interfere with efficacy. ## Methods: rhGAA‐specific T‐cell responses were examined at different time‐points in 6 Hungarian patients treated with rhGAA and compar
✦ LIBER ✦
How common is misdiagnosis in late-onset pompe disease?
✍ Scribed by Lisa D. Hobson-Webb; Priya S. Kishnani
- Publisher
- John Wiley and Sons
- Year
- 2012
- Tongue
- English
- Weight
- 251 KB
- Volume
- 45
- Category
- Article
- ISSN
- 0148-639X
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