Gene transfer vector biodistribution: pivotal safety studies in clinical gene therapy development

Biodistribution and safety studies of hD

Biodistribution and safety studies of hDel-1 plasmid-based gene therapy in mouse and rabbit models

✍ A. Quezada; M. French; J. Perrard; R. Durland; M. Coleman; J. Larson; R. Ponce 📂 Article 📅 2004 🏛 Pharmaceutical Press 🌐 English ⚖ 232 KB

[Methods in Enzymology] Gene Transfer Ve

[Methods in Enzymology] Gene Transfer Vectors for Clinical Application Volume 507 || Gene Therapy for Chronic Granulomatous Disease

✍ Kang, Elizabeth M. 📂 Article 📅 2012 🏛 Elsevier 🌐 English ⚖ 415 KB

This volume of Methods in Enzymology looks at Gene Transfer Vectors for Clinical Application. The chapters provide an invaluable resource for academics, researchers and students alike. With an international board of authors, this volume covers such topics as General principles of retrovirus vector d

[Advances in Biochemical Engineering/Bio

[Advances in Biochemical Engineering/Biotechnology] Gene Therapy and Gene Delivery Systems Volume 99 || Adeno-associated Virus as a Gene Therapy Vector: Vector Development, Production and Clinical Applications

✍ Schaffer, David V.; Zhou, Weichang 📂 Article 📅 2005 🏛 Springer-Verlag ⚖ 139 KB

[Methods in Enzymology] Gene Transfer Ve

[Methods in Enzymology] Gene Transfer Vectors for Clinical Application Volume 507 || Developing Novel Lentiviral Vectors into Clinical Products

✍ Leath, Anna 📂 Article 📅 2012 🏛 Elsevier 🌐 English ⚖ 322 KB

This volume of Methods in Enzymology looks at Gene Transfer Vectors for Clinical Application. The chapters provide an invaluable resource for academics, researchers and students alike. With an international board of authors, this volume covers such topics as General principles of retrovirus vector d

Biodistribution study of phosphonolipids

Biodistribution study of phosphonolipids: a class of non-viral vectors efficient in mice lung-directed gene transfer

✍ P. Delépine; C. Guillaume; T. Montier; J. C. Clément; J. J. Yaouanc; H. Des Abba 📂 Article 📅 2003 🏛 John Wiley and Sons 🌐 English ⚖ 188 KB

## Abstract ## Background A multitude of cationic lipids have been synthesized since they were first proposed for use in gene therapy. Cationic lipids are able to efficiently transfect cells both __in vitro__ and __in vivo.__ Whereas most research groups have focused their investigations on the to

[Methods in Enzymology] Gene Transfer Ve

[Methods in Enzymology] Gene Transfer Vectors for Clinical Application Volume 507 || Analysis of the Clonal Repertoire of Gene-Corrected Cells in Gene Therapy

✍ Paruzynski, Anna 📂 Article 📅 2012 🏛 Elsevier 🌐 English ⚖ 248 KB

This volume of Methods in Enzymology looks at Gene Transfer Vectors for Clinical Application. The chapters provide an invaluable resource for academics, researchers and students alike. With an international board of authors, this volume covers such topics as General principles of retrovirus vector d