Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency
โ Scribed by Aiuti, Alessandro; Cattaneo, Federica; Galimberti, Stefania; Benninghoff, Ulrike; Cassani, Barbara; Callegaro, Luciano; Scaramuzza, Samantha; Andolfi, Grazia; Mirolo, Massimiliano; Brigida, Immacolata; Tabucchi, Antonella; Carlucci, Filippo; Eibl, Martha; Aker, Memet; Slavin, Shimon; Al-Mousa, Hamoud; Al Ghonaium, Abdulaziz; Ferster, Alina; Duppenthaler, Andrea; Notarangelo, Luigi; Wintergerst, Uwe; Buckley, Rebecca H.; Bregni, Marco; Marktel, Sarah; Valsecchi, Maria Grazia; Rossi, Paolo; Ciceri, Fabio; Miniero, Roberto; Bordignon, Claudio; Roncarolo, Maria-Grazia
- Book ID
- 120321930
- Publisher
- Massachusetts Medical Society
- Year
- 2009
- Tongue
- English
- Weight
- 535 KB
- Volume
- 360
- Category
- Article
- ISSN
- 0096-6762
No coin nor oath required. For personal study only.
๐ SIMILAR VOLUMES
Patients with severe combined immunodeficiency disease represent a model for the first clinical applications of gene therapy. Present attempts use insertion of the human adenosine deaminase gene into the peripheral blood T lymphocytes of patients who lack this gene. The ultimate treatment, however,