Efficacy of Sapropterin Dihydrochloride in Increasing Phenylalanine Tolerance in Children with Phenylketonuria: A Phase III, Randomized, Double-Blind, Placebo-Controlled Study

✍ Scribed by Friedrich K. Trefz; Barbara K. Burton; Nicola Longo; Mercedes Martinez-Pardo Casanova; Daniel J. Gruskin; Alex Dorenbaum; Emil D. Kakkis; Eric A. Crombez; Dorothy K. Grange; Paul Harmatz; Mark H. Lipson; Andrzej Milanowski; Linda Marie Randolph; Jerry Vockley; Chester B. Whitley; Jon A. Wolff; Judith Bebchuk; Heidi Christ-Schmidt; Julia B. Hennermann

• Book ID: 113745063
• Publisher: Elsevier Science
• Year: 2009
• Tongue: English
• Weight: 505 KB
• Volume: 154
• Category: Article
• ISSN: 1097-6833
• DOI: 10.1016/j.jpeds.2008.11.040