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Efficacy of Miglustat in Niemann–Pick C disease: A single centre experience

✍ Scribed by Ginocchio, Virginia Maria; D'Amico, Adele; Bertini, Enrico; Ceravolo, Ferdinando; Dardis, Andrea; Verrigni, Daniela; Bembi, Bruno; Dionisi-Vici, Carlo; Deodato, Federica

Book ID: 123439018
Publisher: Elsevier Science
Year: 2013
Tongue: English
Weight: 533 KB
Volume: 110
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2013.07.019

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