Clinical experience with miglustat therapy in pediatric patients with Niemann–Pick disease type C: A case series

✍ Scribed by M. Pineda; M.S. Perez-Poyato; M. O’Callaghan; M.A. Vilaseca; M. Pocovi; R. Domingo; L. Ruiz Portal; A. Verdú Pérez; T. Temudo; A. Gaspar; J.J. Garcia Peñas; S. Roldán; L. Martín Fumero; O. Blanco de la Barca; M.T. García Silva; J. Macías-Vidal; M.J. Coll

• Book ID: 116988916
• Publisher: Elsevier Science
• Year: 2010
• Tongue: English
• Weight: 317 KB
• Volume: 99
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2009.11.007