Duchenne muscular dystrophy (DMD) is a fatal disorder affecting approximately 1 in 3500 live born males, characterized by progressive muscle weakness. Several different strategies are being investigated in developing a cure for this disorder. Until a cure is found, therapeutic and supportive care is
✦ LIBER ✦
Challenges to oligonucleotides-based therapeutics for Duchenne muscular dystrophy
✍ Scribed by Aurélie Goyenvalle; Kay E Davies
- Book ID
- 115028001
- Publisher
- BioMed Central
- Year
- 2011
- Tongue
- English
- Weight
- 230 KB
- Volume
- 1
- Category
- Article
- ISSN
- 2044-5040
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## Abstract Mutations in the dystrophin gene cause an X‐linked genetic disorder: Duchenne muscular dystrophy (DMD). Stem cell therapy is an attractive method to treat DMD because a small number of cells are required to obtain a therapeutic effect. Here, we discussed about multiple types of myogenic
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