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A patient and family perspective on gene therapy for rare diseases

✍ Scribed by Alastair Kent; Cor Oosterwijk


Publisher
John Wiley and Sons
Year
2007
Tongue
English
Weight
44 KB
Volume
9
Category
Article
ISSN
1099-498X

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✦ Synopsis


Abstract

The authors describe the view of patients and patient organisations on gene therapy research and gene therapy regulations. In particular, the added value of partnership between scientists and patient organisations, and patient involvement in the gene therapy field, are addressed. Copyright Β© 2007 John Wiley & Sons, Ltd.


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