A patient and family perspective on gene therapy for rare diseases
β Scribed by Alastair Kent; Cor Oosterwijk
- Publisher
- John Wiley and Sons
- Year
- 2007
- Tongue
- English
- Weight
- 44 KB
- Volume
- 9
- Category
- Article
- ISSN
- 1099-498X
- DOI
- 10.1002/jgm.1097
No coin nor oath required. For personal study only.
β¦ Synopsis
Abstract
The authors describe the view of patients and patient organisations on gene therapy research and gene therapy regulations. In particular, the added value of partnership between scientists and patient organisations, and patient involvement in the gene therapy field, are addressed. Copyright Β© 2007 John Wiley & Sons, Ltd.
π SIMILAR VOLUMES
In two related studies about unconventional cancer therapies, patients and physicians were interviewed about their experiences and opinions. In this paper comparisons are made and implications discussed. There was general agreement among physicians and patients about the importance of providing acce
Linkage data from 92 FAD kindreds were analyzed by lod score analysis under various assumptions of disease penetrance, marker allele frequencies, and heterogeneity. Multilocus linkage analysis supports the existence of a gene in 40%-65% of families with predominantly late-onset illness (after age 65
Dr. Sonis has served as a consultant for Biomodels and Affiliates, LLC (Wellesley, MA). Dr. Elting has received speaker's honoraria from McNeill Pharmaceuticals and Endo Pharmaceuticals (Chadds Ford, PA). Dr. Keefe has received research funding and speaker's honoraria from Amgen. Dr. Peterson has se
## Communicated by A. Jamie Cuticchia We describe a revised and expanded database on human intermediate filament proteins, a major component of the eukaryotic cytoskeleton. The family of 70 intermediate filament genes (including those encoding keratins, desmins, and lamins) is now known to be asso