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A multi-national, randomized, double-blind, placebo-controlled study to evaluate the efficacy and safety of BMN 110 treatment for mucopolysaccharidosis IVA (Morquio syndrome type A)

✍ Scribed by Hendriksz, Christian; Burton, Barbara K.; Fleming, Thomas; Giugliani, Roberto; Harmatz, Paul; Hughes, Derralynn; Jones, Simon; Lin, Shuan-Pei; Mengel, Karl Eugen; Scarpa, Maurizio; Valayannopoulos, Vassili

Book ID: 122094666
Publisher: Elsevier Science
Year: 2013
Tongue: English
Weight: 65 KB
Volume: 108
Category: Article
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2012.11.110

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