Long Term Outcomes of a Phase 1/2, Multicenter, Open-Label, Dose-Escalation Study to Evaluate the Safety, Tolerability, and Efficacy of BMN 110 in Patients with Mucopolysaccharidosis IVA (Morquio A Syndrome)

✍ Scribed by Christian Hendriksz; Ashok Vellodi; Simon Jones; Hiwot Takkele; S. Lee; Sarah Chesler; Celeste Decker

• Book ID: 116989562
• Publisher: Elsevier Science
• Year: 2012
• Tongue: English
• Weight: 57 KB
• Volume: 105
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2011.11.076