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Treatment of Late Infantile Neuronal Ceroid Lipofuscinosis by CNS Administration of a Serotype 2 Adeno-Associated Virus Expressing CLN2 cDNA

✍ Scribed by Worgall, Stefan; Sondhi, Dolan; Hackett, Neil R.; Kosofsky, Barry; Kekatpure, Minal V.; Neyzi, Nurunisa; Dyke, Jonathan P.; Ballon, Douglas; Heier, Linda; Greenwald, Bruce M.; Christos, Paul; Mazumdar, Madhu; Souweidane, Mark M.; Kaplitt, Michael G.; Crystal, Ronald G.

Book ID: 124054679
Publisher: Mary Ann Liebert
Year: 2008
Tongue: English
Weight: 360 KB
Volume: 19
Category: Article
ISSN: 1043-0342
DOI: 10.1089/hum.2008.022

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