The emerging natural history of cross-reactive immunologic material (CRIM)-negative infantile Pompe disease patients treated with recombinant human GAA

✍ Scribed by Sheets, Kathryn B.; Kishnani, Priya S.; Kazi, Zoheb; DeArmey, Stephanie M.; Bali, Deeksha S.; Dai, Jian; Rehder, Catherine W.

• Book ID: 122147520
• Publisher: Elsevier Science
• Year: 2014
• Tongue: English
• Weight: 103 KB
• Volume: 111
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2013.12.237