Severe combined immunodeficiency disease
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Robertson Parkman; Erwin W Gelfand
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Article
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1991
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Elsevier Science
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English
β 741 KB
Patients with severe combined immunodeficiency disease represent a model for the first clinical applications of gene therapy. Present attempts use insertion of the human adenosine deaminase gene into the peripheral blood T lymphocytes of patients who lack this gene. The ultimate treatment, however,