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Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)

✍ Scribed by Randy J. Chandler; Charles P. Venditti


Book ID
118507193
Publisher
Elsevier Science
Year
2012
Tongue
English
Weight
239 KB
Volume
107
Category
Article
ISSN
1096-7192

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