✦ LIBER ✦

Plasmid-based gene transfer ameliorates visceral storage in a mouse model of Sandhoff disease

✍ Scribed by Akira Yamaguchi; Kayoko Katsuyama; Kyoko Suzuki; Kenji Kosaka; Ichiro Aoki; Shoji Yamanaka

Publisher: Springer
Year: 2003
Tongue: English
Weight: 449 KB
Volume: 81
Category: Article
ISSN: 0946-2716
DOI: 10.1007/s00109-002-0410-y

No coin nor oath required. For personal study only.

📜 SIMILAR VOLUMES

AAV8-mediated expression of glucocerebro

AAV8-mediated expression of glucocerebrosidase ameliorates the storage pathology in the visceral organs of a mouse model of Gaucher disease

✍ Kerry Anne McEachern; Jennifer B. Nietupski; Wei-Lien Chuang; Donna Armentano; J 📂 Article 📅 2006 🏛 John Wiley and Sons 🌐 English ⚖ 422 KB

## Abstract ## Background Gaucher disease is the most common of the lysosomal storage disorders. The primary manifestation is the accumulation of glucosylceramide (GL‐1) in the macrophages of liver and spleen (Gaucher cells), due to a deficiency in the lysosomal hydrolase glucocerebrosidase (GC).

Adenovirus-mediated gene therapy in a mo

Adenovirus-mediated gene therapy in a mouse model of glycogen storage disease type 1a

✍ Janice Chou; Adriana Zingone; Chi-Jiunn Pan 📂 Article 📅 2002 🏛 Springer 🌐 English ⚖ 259 KB

Marrow Stromal Cell-Based Cyclooxygenase

Marrow Stromal Cell-Based Cyclooxygenase 2 Ex Vivo Gene-Transfer Strategy Surprisingly Lacks Bone-Regeneration Effects and Suppresses the Bone-Regeneration Action of Bone Morphogenetic Protein 4 in a Mouse Critical-Sized Calvarial Defect Model

✍ K.-H. William Lau; Reinhard Gysin; Shin-Tai Chen; Jon E. Wergedal; David J. Bayl 📂 Article 📅 2009 🏛 Springer 🌐 English ⚖ 471 KB