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Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

✍ Scribed by Bowles, Dawn E; McPhee, Scott WJ; Li, Chengwen; Gray, Steven J; Samulski, Jade J; Camp, Angelique S; Li, Juan; Wang, Bing; Monahan, Paul E; Rabinowitz, Joseph E

Book ID: 115538497
Publisher: Nature Publishing Group
Year: 2012
Tongue: English
Weight: 688 KB
Volume: 20
Category: Article
ISSN: 1525-0016
DOI: 10.1038/mt.2011.237

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