✦ LIBER ✦

P03 Exon skipping and dystrophin restoration in Duchenne muscular dystrophy patients after systemic phosphorodiamidate morpholino oligomer treatment

✍ Scribed by S. Cirak; V. Arechavala-Gomeza; M. Guglieri; L. Feng; S. Torelli; K. Anthony; M.E. Garralda; D. Wells; G. Dickson; M.J.A. Wood; S.D. Wilton; V. Straub; S.B. Shrewsbury; C. Sewry; J.E. Morgan; K. Bushby; F. Muntoni

Book ID: 117670322
Publisher: Elsevier Science
Year: 2011
Tongue: English
Weight: 92 KB
Volume: 21
Category: Article
ISSN: 0960-8966
DOI: 10.1016/s0960-8966(11)70022-0

No coin nor oath required. For personal study only.

📜 SIMILAR VOLUMES

1FC2.1 Exon skipping and dystrophin rest

1FC2.1 Exon skipping and dystrophin restoration in Duchenne Muscular Dystrophy patients after systemic phosphorodiamidate morpholino oligomer treatment

✍ S. Cirak; V. Arechavala-Gomeza; M. Guglieri; L. Feng; S. Torelli; K. Anthony; M. 📂 Article 📅 2011 🏛 Elsevier Science 🌐 English ⚖ 37 KB

P01 Current progress with the systemic a

P01 Current progress with the systemic administration trial of AVI-4658, a novel Phosphorodiamidate Morpholino Oligomer (PMO) skipping dystrophin exon 51 in Duchenne muscular dystrophy (DMD)

✍ S. Cirak; M. Guglieri; S. Shrewsbury; K. Bushby; F. Muntoni 📂 Article 📅 2010 🏛 Elsevier Science 🌐 English ⚖ 83 KB

P3.07 Preclinical safety of AVI-4658, a

P3.07 Preclinical safety of AVI-4658, a phosphorodiamidate morpholino oligomer (PMO) being developed to skip exon 51 in Duchenne muscular dystrophy

✍ S.B. Shrewsbury; P. Sazani 📂 Article 📅 2010 🏛 Elsevier Science 🌐 English ⚖ 47 KB

O.16 Current progress and preliminary re

O.16 Current progress and preliminary results with the systemic administration trial of AVI-4658, a novel phosphorodiamidate morpholino oligomer (PMO) skipping dystrophin exon 51 in Duchenne muscular dystrophy (DMD)

✍ S.B. Shrewsbury; S. Cirak; M. Guglieri; K. Bushby; F. Muntoni 📂 Article 📅 2010 🏛 Elsevier Science 🌐 English ⚖ 48 KB

P3.01 Antisense RNA/ethylene-bridged nuc

P3.01 Antisense RNA/ethylene-bridged nucleic acids chimera induces exon 45 skipping and restores dystrophin expression in myocytes of Duchenne muscular dystrophy

✍ M. Yagi; M. Ota; H. Awano; Y. Takeshima; M. Matsuo 📂 Article 📅 2010 🏛 Elsevier Science 🌐 English ⚖ 49 KB

T.P.1.02 Importance of checking exon ski

T.P.1.02 Importance of checking exon skipping events prior to clinical trials using systemically delivered antisense morpholino in Duchenne muscular dystrophy patients

✍ S. Nakono; S. Ozasa; H. Kosuge; K. Nomura; I. Fujii; K. Ito; M. Matsukura; S. Ki 📂 Article 📅 2009 🏛 Elsevier Science 🌐 English ⚖ 39 KB