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NIHRAC and FDA ponder gene-therapy risks

✍ Scribed by Fox, Jeffrey L.


Book ID
109901216
Publisher
Nature Publishing Group
Year
1993
Tongue
English
Weight
227 KB
Volume
11
Category
Article
ISSN
1087-0156

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## Abstract Hemophilia is an inherited bleeding disorder caused by a deficiency of functional clotting factors VIII or IX in the blood plasma. The drawbacks of the classical protein substitution therapy fueled interest in alternative treatments by gene therapy. Hemophilia has been recognized as an