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Longitudinal data from the international registry for Niemann-Pick disease type C (NPC)

✍ Scribed by Patterson, Marc C.; Mengel, Eugen; Wijburg, Frits A.; Vanier, Marie T.; Schwierin, Barbara; Muller, Audrey; Drevon, Harir; Pineda, Merce

No coin nor oath required. For personal study only.

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