Long-term follow-up of endurance and safety outcomes during enzyme replacement therapy for mucopolysaccharidosis VI: Final results of three clinical studies of recombinant human N-acetylgalactosamine 4-sulfatase

✍ Scribed by Paul Harmatz; Roberto Giugliani; Ida Vanessa D. Schwartz; Nathalie Guffon; Elisa Leão Teles; M. Clara Sá Miranda; J. Edmond Wraith; Michael Beck; Laila Arash; Maurizio Scarpa; David Ketteridge; John J. Hopwood; Barbara Plecko; Robert Steiner; Chester B. Whitley; Paige Kaplan; Zi-Fan Yu; Stuart J. Swiedler; Celeste Decker

• Book ID: 118507102
• Publisher: Elsevier Science
• Year: 2008
• Tongue: English
• Weight: 420 KB
• Volume: 94
• Category: Article
• ISSN: 1096-7192
• DOI: 10.1016/j.ymgme.2008.04.001