Long-term experience with enzyme replacement therapy (ERT) in MPS II patients with a severe phenotype: an international case series

✍ Scribed by Lampe, Christina; Bosserhoff, Ann-Kathrin; Burton, Barbara K.; Giugliani, Roberto; de Souza, Carolina F.; Bittar, Camila; Muschol, Nicole; Olson, Rebecca; Mendelsohn, Nancy J.

• Book ID: 121745627
• Publisher: Springer
• Year: 2014
• Tongue: English
• Weight: 206 KB
• Volume: 37
• Category: Article
• ISSN: 0141-8955
• DOI: 10.1007/s10545-014-9686-7