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Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

✍ Scribed by Maria Kinali; Virginia Arechavala-Gomeza; Lucy Feng; Sebahattin Cirak; David Hunt; Carl Adkin; Michela Guglieri; Emma Ashton; Stephen Abbs; Petros Nihoyannopoulos; Maria Elena Garralda; Mary Rutherford; Caroline Mcculley; Linda Popplewell; Ian R Graham; George Dickson; Matthew JA Wood; Dominic J Wells; Steve D Wilton; Ryszard Kole; Volker Straub; Kate Bushby; Caroline Sewry; Jennifer E Morgan; Francesco Muntoni

Book ID: 114409291
Publisher: The Lancet
Year: 2009
Tongue: English
Weight: 610 KB
Volume: 8
Category: Article
ISSN: 1474-4465
DOI: 10.1016/s1474-4422(09)70211-x

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