Restricted transgene persistence after l
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Rafael Moreno; Marta Rosal; Itziar Martinez; Felip Vilardell; Juan Ramón Gonzale
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Article
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2008
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John Wiley and Sons
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English
⚖ 353 KB
## Abstract ## Background Prenatal gene transfer may enable early causal intervention for the treatment or prevention of many devastating diseases. Nevertheless, permanent correction of most inherited disorders requires a sustained level of expression from the therapeutic transgene, which could th