Kinetics of 57Co-bleomycin in mice after intravenous, subcutaneous and intratumoral injection

Glycogen storage in multiple muscles of

Glycogen storage in multiple muscles of old GSD-II mice can be rapidly cleared after a single intravenous injection with a modified adenoviral vector expressing hGAA

✍ Fang Xu; Enyu Ding; Felicia Migone; Delila Serra; Ayn Schneider; Yuan-Tsong Chen 📂 Article 📅 2005 🏛 John Wiley and Sons 🌐 English ⚖ 248 KB

Background Glycogen storage disease II (GSD-II) is an autosomal recessive lysosomal storage disease, due to acid-alpha-glucosidase (GAA) deficiency. The disease is characterized by massive glycogen accumulation in the cardiac and skeletal muscles. There is early onset (infantile, also known as Pompe