𝔖 Bobbio Scriptorium
✦   LIBER   ✦

Gene therapy/cell therapy for lysosomal storage disease

✍ Scribed by Y. Eto; T. Ohashi


Book ID
110228308
Publisher
Springer
Year
2000
Tongue
English
Weight
64 KB
Volume
23
Category
Article
ISSN
0141-8955

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## Abstract There are more than 40 different forms of inherited lysosomal storage diseases (LSDs) known to occur in humans and the aggregate incidence has been estimated to approach 1 in 7000 live births. Most LSDs are associated with high morbidity and mortality and represent a significant burden