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Gaucher disease due to saposin C deficiency, previously described as non-neuronopathic form — No positive effects after 2-years of miglustat therapy

✍ Scribed by Anna Tylki-Szymańska; Johanna E.M. Groener; Marek Leszek Kamiński; Agnieszka Ługowska; Elżbieta Jurkiewicz; Barbara Czartoryska


Book ID
116989448
Publisher
Elsevier Science
Year
2011
Tongue
English
Weight
301 KB
Volume
104
Category
Article
ISSN
1096-7192

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